Title: The Leader in RNA-based Medicine | Sarepta Therapeutics
Description: We develop RNA-based therapeutics to improve the lives of people affected by serious diseases; this includes eteplirsen for the treatment of DMD.
Description: DNA Learning Center's multimedia guide to genetic disorders. Info on symptoms, cause, inheritance, and treatment. First-hand accounts from doctors and patients.
Description: Duchenne Parent Project wil beter en sneller onderzoek naar Duchenne Spierdystrofie (Duchenne Muscular Dystrophy). Om medicijnen te ontwikkelen die de afbraak van spieren kunnen vertragen en stoppen. En om een betere behandeling en hulpmiddelen te ontwik